Gel-mediated delivery of AAV1 vectors corrects ventilatory function in pompe mice with established disease

Cathryn S. Mah, Darin J. Falk, Sean A. Germain, Jeffry S. Kelley, Melissa A. Lewis, Denise A. Cloutier, Lara R. Deruisseau, Thomas J. Conlon, Kerry O. Cresawn, Thomas J. Fraites, Martha Campbell-Thompson, David D. Fuller, Barry J. Byrne

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)502-510
Number of pages9
JournalMolecular Therapy
Volume18
Issue number3
DOIs
StatePublished - Mar 2010
Externally publishedYes

ASJC Scopus Subject Areas

  • Molecular Medicine
  • Molecular Biology
  • Genetics
  • Pharmacology
  • Drug Discovery

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