Gel-mediated delivery of AAV1 vectors corrects ventilatory function in pompe mice with established disease

  • Cathryn S. Mah
  • , Darin J. Falk
  • , Sean A. Germain
  • , Jeffry S. Kelley
  • , Melissa A. Lewis
  • , Denise A. Cloutier
  • , Lara R. Deruisseau
  • , Thomas J. Conlon
  • , Kerry O. Cresawn
  • , Thomas J. Fraites
  • , Martha Campbell-Thompson
  • , David D. Fuller
  • , Barry J. Byrne

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)502-510
Number of pages9
JournalMolecular Therapy
Volume18
Issue number3
DOIs
StatePublished - Mar 2010
Externally publishedYes

ASJC Scopus Subject Areas

  • Molecular Medicine
  • Molecular Biology
  • Genetics
  • Pharmacology
  • Drug Discovery

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