Physiological correction of pompe disease by systemic delivery of adeno-associated virus serotype 1 vectors

Cathryn Mah, Christina A. Pacak, Kerry O. Cresawn, Lara R. DeRuisseau, Sean Germain, Melissa A. Lewis, Denise A. Cloutier, David D. Fuller, Barry J. Byrne

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)501-507
Number of pages7
JournalMolecular Therapy
Volume15
Issue number3
DOIs
StatePublished - Mar 2007
Externally publishedYes

ASJC Scopus Subject Areas

  • Molecular Medicine
  • Molecular Biology
  • Genetics
  • Pharmacology
  • Drug Discovery

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