Physiological correction of pompe disease by systemic delivery of adeno-associated virus serotype 1 vectors

  • Cathryn Mah
  • , Christina A. Pacak
  • , Kerry O. Cresawn
  • , Lara R. DeRuisseau
  • , Sean Germain
  • , Melissa A. Lewis
  • , Denise A. Cloutier
  • , David D. Fuller
  • , Barry J. Byrne

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)501-507
Number of pages7
JournalMolecular Therapy
Volume15
Issue number3
DOIs
StatePublished - Mar 2007
Externally publishedYes

ASJC Scopus Subject Areas

  • Molecular Medicine
  • Molecular Biology
  • Genetics
  • Pharmacology
  • Drug Discovery

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